Biomarkers Landmark-class

PD-L1 immunohistochemistry: current state and challenges as a companion diagnostic

This comprehensive review examines PD-L1 as the most widely validated biomarker for selecting patients for anti-PD-1/PD-L1 therapy, while detailing persistent challenges including inter-assay variability, different companion diagnostic requirements per drug, inconsistent cut-off points, and lack of prospective cross-assay comparisons. The authors discuss regulatory complexities and how future quantitative methods could improve patient selection. Essential reading for pathology labs running PD-L1 testing.

The original study

PD-L1 as a biomarker of response to immune-checkpoint inhibitors.

Authors
Doroshow DB, Bhalla S, Beasley MB, Sholl LM, Kerr KM, Gnjatic S, et al.
Journal
Nature reviews. Clinical oncology
Type
Journal Article, Review
PMID
33580222
Read the original study →

Original abstract

Immune-checkpoint inhibitors targeting PD-1 or PD-L1 have already substantially improved the outcomes of patients with many types of cancer, although only 20-40% of patients derive benefit from these new therapies. PD-L1, quantified using immunohistochemistry assays, is currently the most widely validated, used and accepted biomarker to guide the selection of patients to receive anti-PD-1 or anti-PD-L1 antibodies. However, many challenges remain in the clinical use of these assays, including the necessity of using different companion diagnostic assays for specific agents, high levels of inter-assay variability in terms of both performance and cut-off points, and a lack of prospective comparisons of how PD-L1+ disease diagnosed using each assay relates to clinical outcomes. In this Review, we describe the current role of PD-L1 immunohistochemistry assays used to inform the selection of patients to receive anti-PD-1 or anti-PD-L1 antibodies, we discuss the various technical and clinical challenges associated with these assays, including regulatory issues, and we provide some perspective on how to optimize PD-L1 as a selection biomarker for the future treatment of patients with solid tumours.